2026년 서울대학교 바이오인공지능연구단 2월 초청세미나

Matthew H. Porteus 교수 (Stanford University)

: The Future of Cell and Gene Therapy

Matthew Porteus at Stanford University developed a highly efficient method for gene  editing by using Adeno-associated virus serotype 6 (AAV6) as a donor template delivery vehicle combined with CRISPR/Cas9. This approach, particularly using AAV6, significantly increased targeted integration (homology-directed repair) in blood stem cells to 30–50% for treating diseases like sickle cell. In this talk, Pf Porteus will be discussing about the future of gene therapy focusing on AAV based gene delivery system.